Generating RWE in Spinal Muscular Atrophy (SMA) faces hurdles due to evolving standard of care with recent treatments, inconsistent outcomes measurement due to age at treatment initiation and severity baseline, and the need for long-term follow-up.

We invite you to test the following research objectives with us:

  • Patient characteristics and long-term outcomes
  • Neurodevelopment and pathophysiology
  • Evolving standard of care and treatment
  • Long-term safety and durability
  • Healthcare resource utilization (HCRU)

Email us at contact@lumanity.com to discuss your research needs.

Download our one-pager

Complete the form to download our one-pager on Spinal Muscular Atrophy

"*" indicates required fields

This field is for validation purposes and should be left unchanged.
Sign me up to receive regular insights from Lumanity
By selecting this box, I consent to receive Lumanity marketing communications by email.